Phase I/II study of intrapleural administration of a Serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-Antitrypsin cDNA to individuals with α1-Antitrypsin deficiency

Maria J. Chiuchiolo, Stephen M. Kaminsky, Dolan Sondhi, Denesy Mancenido, Charleen Hollmann, Ronald Crystal

Research output: Contribution to journalArticle

11 Citations (Scopus)
Original languageEnglish
Pages (from-to)112-133
Number of pages22
JournalHuman Gene Therapy Clinical Development
Volume25
Issue number3
DOIs
Publication statusPublished - 1 Jan 2014
Externally publishedYes

Fingerprint

Gene Transfer Techniques
Genetic Vectors
Dependovirus
alpha 1-Antitrypsin
Genetic Therapy
Cohort Studies
Complementary DNA
Genes
Serogroup

ASJC Scopus subject areas

  • Genetics(clinical)

Cite this

Phase I/II study of intrapleural administration of a Serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-Antitrypsin cDNA to individuals with α1-Antitrypsin deficiency. / Chiuchiolo, Maria J.; Kaminsky, Stephen M.; Sondhi, Dolan; Mancenido, Denesy; Hollmann, Charleen; Crystal, Ronald.

In: Human Gene Therapy Clinical Development, Vol. 25, No. 3, 01.01.2014, p. 112-133.

Research output: Contribution to journalArticle

@article{cca2134c23624a70805d9a124e682f1e,
title = "Phase I/II study of intrapleural administration of a Serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-Antitrypsin cDNA to individuals with α1-Antitrypsin deficiency",
author = "Chiuchiolo, {Maria J.} and Kaminsky, {Stephen M.} and Dolan Sondhi and Denesy Mancenido and Charleen Hollmann and Ronald Crystal",
year = "2014",
month = "1",
day = "1",
doi = "10.1089/humc.2014.2513",
language = "English",
volume = "25",
pages = "112--133",
journal = "Human gene therapy. Clinical development",
issn = "2324-8637",
publisher = "Mary Ann Liebert Inc.",
number = "3",

}

TY - JOUR

T1 - Phase I/II study of intrapleural administration of a Serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-Antitrypsin cDNA to individuals with α1-Antitrypsin deficiency

AU - Chiuchiolo, Maria J.

AU - Kaminsky, Stephen M.

AU - Sondhi, Dolan

AU - Mancenido, Denesy

AU - Hollmann, Charleen

AU - Crystal, Ronald

PY - 2014/1/1

Y1 - 2014/1/1

UR - http://www.scopus.com/inward/record.url?scp=84907259251&partnerID=8YFLogxK

UR - http://www.scopus.com/inward/citedby.url?scp=84907259251&partnerID=8YFLogxK

U2 - 10.1089/humc.2014.2513

DO - 10.1089/humc.2014.2513

M3 - Article

C2 - 25238276

AN - SCOPUS:84907259251

VL - 25

SP - 112

EP - 133

JO - Human gene therapy. Clinical development

JF - Human gene therapy. Clinical development

SN - 2324-8637

IS - 3

ER -