• 65820 Citations
  • 132 h-Index
1969 …2020

Research output per year

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Research Output

Anti-Phospho-Tau Gene Therapy for Chronic Traumatic Encephalopathy

Sacramento, C. B., Sondhi, D., Rosenberg, J. B., Chen, A., Giordano, S., Pey, E., Lee, V., Stiles, K. M., Havlicek, D. F., Leopold, P. L., Kaminsky, S. M. & Crystal, R. G., Jan 2020, In : Human gene therapy. 31, 1-2, p. 57-69 13 p.

Research output: Contribution to journalArticle

Open Access
  • 1 Citation (Scopus)

    Symmetric Age Association of Retinal Degeneration in Patients with CLN2-Associated Batten Disease

    Kovacs, K. D., Patel, S., Orlin, A., Kim, K., Van Everen, S., Conner, T., Sondhi, D., Kaminsky, S. M., D'Amico, D. J., Crystal, R. G. & Kiss, S., 1 Jan 2020, (Accepted/In press) In : Ophthalmology Retina.

    Research output: Contribution to journalArticle

    Open Access
  • Systemic Adeno-Associated Virus-Mediated Gene Therapy Prevents the Multiorgan Disorders Associated with Aldehyde Dehydrogenase 2 Deficiency and Chronic Ethanol Ingestion

    Matsumura, Y., Li, N., Alwaseem, H., Pagovich, O. E., Crystal, R. G., Greenblatt, M. B. & Stiles, K. M., Feb 2020, In : Human gene therapy. 31, 3-4, p. 163-182 20 p.

    Research output: Contribution to journalArticle

    Open Access
  • Advances in the treatment of neuronal ceroid lipofuscinosis

    Rosenberg, J. B., Chen, A., Kaminsky, S. M., Crystal, R. G. & Sondhi, D., 2 Nov 2019, In : Expert Opinion on Orphan Drugs. 7, 11, p. 473-500 28 p.

    Research output: Contribution to journalReview article

  • Characterization of an immortalized human small airway basal stem/progenitor cell line with airway region-specific differentiation capacity

    Wang, G., Lou, H. H., Salit, J., Leopold, P. L., Driscoll, S., Schymeinsky, J., Quast, K., Visvanathan, S., Fine, J. S., Thomas, M. J. & Crystal, R., 23 Aug 2019, In : Respiratory Research. 20, 1, 196.

    Research output: Contribution to journalArticle

    Open Access